Thrombosis and Haemostasis, Inhaltsverzeichnis Thromb Haemost 1997; 78(01): 031-036DOI: 10.1055/s-0038-1657496 Gene therapy for hemophilia: hopes and reality for the children of the new century Schattauer GmbH Stuttgart Gene Therapy for Hemophilia A Sheila Connelly Department of Molecular and Cell Biology, Genetic Therapy, Inc., Gaithersburg, MD, USA , Michael Kaleko Department of Molecular and Cell Biology, Genetic Therapy, Inc., Gaithersburg, MD, USA › InstitutsangabenArtikel empfehlen Abstract als PDF herunterladen Artikel einzeln kaufen PDF (1345 kb) Referenzen References 1 Sadler JE, Davie EW. Hemophilia A, hemophilia B and von Willebrand’s disease. In: The Molecular Basis of Blood Diseases. Nienhuis AW, Leder P, Majerus PW. eds. W.B Saunders Co; New York: 1987. pp 575-598 2 Aledort L. Inhibitors in hemophilia patients: Current status and management. Am J Hemat 1994; 47: 208-217 3 Lozier JN, Brinkhous KM. Gene therapy and the hemophilias. 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