Neuropediatrics 2019; 50(S 02): S1-S55
DOI: 10.1055/s-0039-1698169
DOI: 10.1055/s-0039-1698169
Oral Presentations
Neuromuscular Diseases and Varia
Onasemnogene Abeparvovec Gene-Replacement Therapy (GRT) in Pre-symptomatic Spinal Muscular Atrophy (SMA): SPR1NT Study Update
Meredith Schultz
1
AveXis, Inc., AveXis, Inc., Bannockburn, Illinois, United States
,
Kathryn J. Swoboda
2
Massachusetts General Hospital, Department of Neurology, Boston, Massachusetts, United
States
,
Michelle Farrar
3
Sydney Children’s Hospital, Department of Neurology, Randwick, Australia
,
Hugh McMillan
4
Children’s Hospital of Eastern Ontario, Department of Pediatrics, Ottawa, Canada
,
Julie Parsons
5
Children’s Hospital Colorado, Department of Neurology, Aurora, Colorado, United States
,
Uwe Ernst
6
AveXis, Inc., Medical Affairs, Bannockburn, Illinois, United States
,
Elaine Kernbauer
7
AveXis, Inc., Clinical Operations, Bannockburn, Illinois, United States
,
Marcia Farrow
6
AveXis, Inc., Medical Affairs, Bannockburn, Illinois, United States
,
Francis G. Ogrinc
8
AveXis, Inc., Biostatistics, Bannockburn, Illinois, United States
,
Sarah Kavanagh
7
AveXis, Inc., Clinical Operations, Bannockburn, Illinois, United States
,
Douglas E. Feltner
7
AveXis, Inc., Clinical Operations, Bannockburn, Illinois, United States
,
Bryan E. McGill
7
AveXis, Inc., Clinical Operations, Bannockburn, Illinois, United States
,
Sidney A. Spector
7
AveXis, Inc., Clinical Operations, Bannockburn, Illinois, United States
,
James L’Italien
9
AveXis, Inc., Regulatory and Quality, Bannockburn, Illinois, United States
,
Douglas Sproule
7
AveXis, Inc., Clinical Operations, Bannockburn, Illinois, United States
,
Kevin Strauss
10
Clinic for Special Children, -, Strasburg, Pennsylvania, United States
› Author Affiliations
