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Osteologie 2021; 30(01): 73
DOI: 10.1055/s-0040-1722141
2. Abstracts

A Global Natural History Study of Fibrodysplasia Ossificans Progressiva (FOP): 12-Month Outcomes

Authors

  • M Al Mukaddam

    1   Departments of Orthopaedic Surgery & Medicine, University of Pennsylvania, Philadelphia, PA, USA, Perelman School of Medicine, The Center for Research in FOP and Related Disorders, Philadelphia
  • C Stockklausner

    2   Klinikum Garmisch-Partenkirchen, Akademisches Lehrkrankenhaus der Ludwig-Maximilians-Universität München (LMU), Kinder- und Jugendmedizin, Garmisch-Partenkirchen
  • RJ Pignolo

    3   Department of Medicine, Mayo Clinic, Rochester, Rochester, MN
  • G Baujat

    4   Département de Génétique, Institut IMAGINE, Hôpital Universitaire Necker-Enfants Malades, Paris, France, Paris
  • MA Brown

    5   King’s College London, Guy’s & St Thomas’ NHS Foundation Trust and King’s College London NIHR Biomedical Research Centre, London
  • C De Cunto

    6   Pediatric Rheumatology SectionDepartment of Pediatrics, Hospital Italiano de Buenos Aires, Buenos Aires
  • M Di Rocco

    7   Unit of Rare Diseases, Department of Pediatrics, Giannina Gaslini Institute, Genoa, Genoa
  • EC Hsiao

    8   7Division of Endocrinology and Metabolism, UCSF Metabolic Bone Clinic, Institute of Human Genetics, University of California-San Francisco, San Francisco, CA
  • R Keen

    9   Royal National Orthopaedic Hospital, Stanmore, Centre for Metabolic Bone Disease, Stanmore
  • K-H Le Quan Sang

    4   Département de Génétique, Institut IMAGINE, Hôpital Universitaire Necker-Enfants Malades, Paris, France, Paris
  • A Strahs

    10   Ipsen Pharma GmbH, Newton, MA
  • R Marino

    10   Ipsen Pharma GmbH, Newton, MA
  • FS Kaplan

    11   Departments of Orthopaedic Surgery & Medicine, The Center for Research in FOP and Related Disorders, Perelman School of Medicine, University of Pennsylvania, Philadelphia, Philadelphia, PA