DOI: 10.1055/s-00000145

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References

Beck M, Hughes D, Kampmann C. et al
Long-term effectiveness of agalsidase alfa enzyme replacement in Fabry disease: A Fabry Outcome Survey analysis.

Mol Genet Metab Rep 2015;
3: 21-27 doi:10.1016/j.ymgmr.2015.02.002

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