DOI: 10.1055/s-00000071

Seminars in Neurology

References

Kinali M, Arechavala-Gomeza V, Feng L , et al.
Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study.

Lancet Neurol 2009;
8 (10) 918-928

Download Bibliographical Data

Search in:
Access: