DOI: 10.1055/s-00000071

Seminars in Neurology

References

Mulders SA, van den Broek WJ, Wheeler TM , et al.
Triplet-repeat oligonucleotide-mediated reversal of RNA toxicity in myotonic dystrophy.

Proc Natl Acad Sci U S A 2009;
106 (33) 13915-13920

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