DOI: 10.1055/s-00029022

Journal of Pediatric Biochemistry

References

Schiffmann R, Murray GJ, Treco D , et al.
Infusion of alpha-galactosidase A reduces tissue globotriaosylceramide storage in patients with Fabry disease.

Proc Natl Acad Sci U S A 2000;
97 (1) 365-370

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