DOI: 10.1055/s-00000041

Neuropediatrics

References

Desai AK, Walters CK, Cope HL, Kazi ZB, DeArmey SM, Kishnani PS.
Enzyme replacement therapy with alglucosidase alfa in Pompe disease: clinical experience with rate escalation.

Mol Genet Metab 2018;
123 (02) 92-96

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