DOI: 10.1055/s-00000041

Neuropediatrics

References

van der Ploeg AT, Kruijshaar ME, Toscano A. et al; European Pompe Consortium.
European consensus for starting and stopping enzyme replacement therapy in adult patients with Pompe disease: a 10-year experience.

Eur J Neurol 2017;
24 (06) 768-e31

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