DOI: 10.1055/s-00000075

Seminars in Respiratory and Critical Care Medicine

References

Keating D, Marigowda G, Burr L. et al; VX16-445-001 Study Group.
VX-445-tezacaftor-ivacaftor in patients with cystic fibrosis and one or two Phe508del alleles.

N Engl J Med 2018;
379 (17) 1612-1620

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