DOI: 10.1055/s-00000075

Seminars in Respiratory and Critical Care Medicine

References

Davies JC, Moskowitz SM, Brown C. et al; VX16-659-101 Study Group.
VX-659-tezacaftor-ivacaftor in patients with cystic fibrosis and one or two Phe508del alleles.

N Engl J Med 2018;
379 (17) 1599-1611

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