DOI: 10.1055/s-00000140

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References

Mercuri E, Darras BT, Chiriboga CA. et al.
Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy.

N Engl J Med 2018;
378: 625-635
doi:10.1056/NEJMoa1710504

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