Stellungnahme von DOG, RG und BVA zur therapeutischen Anwendung von voretigene neparvovec (Luxturna™) in der Augenheilkunde^[*]

Seit dem 23. November 2018 ist das Medikament Luxturna^™ zur Behandlung von Netzhautdystrophien bei Patienten mit biallelischen Mutationen in RPE65 in der Europäischen Union zugelassen. Im Folgenden werden die zwischen der Retinologischen Gesellschaft, der Deutschen Ophthalmologischen Gesellschaft und dem Berufsverband der Augenärzte Deutschlands konsentierten Behandlungsempfehlungen und das Anwendungsspektrum dargelegt.

^* Diese Stellungnahme erscheint ebenfalls in der Zeitschrift Der Ophthalmologe, Springer Verlag, Heidelberg.

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