Efficacy and safety of nusinersen in children with later-onset spinal muscular atrophy (SMA): results of the phase 3 CHERISH study - Kirschner, Jan; Mercuri, Eugenio; Finkel, Richard S.; Chiriboga, Claudia A.; Kuntz, Nancy; Darras, Basil T.; Shieh, Perry B.; Saito, Kayoko; De Vivo, Darryl C.; Mazzone, Elena S.; Montes, Jacqueline; Yang, Qingqing; Zhong, Zhenshao John; Gheuens, Sarah; Bennett, C Frank; Schneider, Eugene; Farwell, Wildon; on behalf of the CHERISH Study Group (Neuropediatrics, 2017)