Effectiveness of Ataluren in Patients with nmDMD: Confirmatory Evidence from the STRIDE Registry - Werner, C.; Gruenert, J.; Mercuri, E.; Buccella, F.; Osorio, A. N.; Tulinius, M.; Desguerre, I.; de Resende, M. B. Dutra; McDonald, C.; Gordish-Dressman, H.; Morgenroth, L.; Johnson, S.; Krolick, A.; Anbu, B.; Liu, E.; Muntoni, F. (Neuropediatrics, 2025)