Trofinetide for the Treatment of Rett Syndrome: Long-Term Safety and Efficacy Results from the Open-Label LILAC and LILAC-2 Studies - Huber, A.; Percy, A.; Neul, J.; Benke, T.; Berry-Kravis, E.; Glaze, D.; Marsh, E.; Bishop, K.; Youakim, J. (Neuropediatrics, 2025)