DOI:
10.1055/s-00000059
Pneumologie
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References
Rowe SM, Daines C, Ringshausen FC. et al.
Tezacaftor–Ivacaftor in Residual-Function Heterozygotes with Cystic Fibrosis.
N Engl J Med 2017;
377: 2024-2035
DOI: 10.1056/NEJMoa1709847.
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