DOI: 10.1055/s-00000041

Neuropediatrics

References

Matzner U, Hartmann D, Lullmann-Rauch R. et al.
Bone marrow stem cell-based gene transfer in a mouse model for metachromatic leukodystrophy: effects on visceral and nervous system disease manifestations. 
Gene Ther 2002; 9: 53-63  

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