DOI : 10.1055/s-00054595

Arquivos de Neuro-Psiquiatria

Issue S 02 · Volume 82 · October 2024 DOI: 10.1055/s-015-61658


18° Congresso Brasileiro de Neurologia Infantil
Tivoli Mofarrej São Paulo - SP, 06.–09.09.2023


A144
McDonald, Craig M.; Carneiro, Ana Paula; Machado, Daiana Suelen; Federhen, Andressa; Trifillis, Panayiota: Ataluren preserves upper limb function in NMDMD patients from study 041, a phase 3 placebo-controlled trial, and the stride registry