DOI: 10.1055/s-00029022

Journal of Pediatric Biochemistry

References

Benjamin ER, Khanna R, Schilling A , et al.
Co-administration with the pharmacological chaperone AT1001 increases recombinant human α-galactosidase A tissue uptake and improves substrate reduction in Fabry mice.

Mol Ther 2012;
20 (4) 717-726

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